Conversation

I received the new gene-editing drug for sickle cell disease. It changed my life. | MIT Technology Review https://www.technologyreview.com/2023/12/04/1084209/vertex-exacel-approval-gene-editing-sickle-cell-disease-patient/ “I’d lived with #SickleCell my whole life—experiencing chronic pain, organ damage, and hopelessness. To me, this opportunity meant finally taking control of my life and having the opportunity to be a present father.

The drug I received, called #ExaCel, could soon become the first #CRISPR-based treatment to win approval from the US Food and Drug Administration,”